How does gene therapy work?: MedlinePlus Genetics
Gene therapy works by altering the genetic code to recover the functions of critical proteins. Discover how this process works.
What Is Gene Therapy? Pros, Cons & Examples - Cleveland Clinic
Jun 17, 2025 · It works by replacing a malfunctioning gene, “turning off” a disease-causing gene or giving you a new copy of a gene. Approved gene therapies treat inherited blood, neuromuscular and …
Gene therapy - Mayo Clinic
Apr 23, 2024 · In this procedure, specialists aim to fix or replace a faulty gene to try to cure a disease or make the body better able to fight a disease.
Gene Therapy Process & Steps
See key steps of the gene therapy treatment process, from consultation through recovery and follow-up.
What is Gene Therapy? | FDA
Human gene therapy is the administration of genetic material to modify or manipulate the expression of a gene product or to alter the biological properties of living cells for therapeutic use.
Gene therapy - Wikipedia
Gene therapy is medical technology that aims to produce a therapeutic effect through the manipulation of gene expression or through altering the biological properties of living cells. [1][2][3]
Gene therapy | Description, Uses, Examples, & Safety Issues ...
Jan 21, 2026 · Some aspects of gene therapy, including genetic manipulation and selection, research on embryonic tissue, and experimentation on human subjects, have aroused ethical controversy and …