Shortly after taking reins at BioMarin, CEO Alexander Hardy laid out three paths the company could take for its struggling ...

Just as Adverum’s cash reserves were running dry, Eli Lilly has swooped in to buy the biotech and its phase 3-stage eye disease gene therapy.

Pivotal results from uniQure’s gene therapy for Huntington’s disease have brought new light to patients who have known only ...

For children born with severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID), an investigational ...

Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the ...

From the 2010s to the present, the existing technologies in the clinic and operating room have been improved with the goals ...

A new gene therapy approach aimed at protecting people with type 1 diabetes from developing diabetic kidney disease—a serious ...

Columnist Jennifer Lynne concludes a series on Domenic Catrine, whose life has improved after receiving gene therapy to treat hemophilia B.

SINGAPORE, SG / ACCESS Newswire / October 22, 2025 / Immortal Dragons, a $40 million longevity fund, announced its strategic investment in Unlimited Bio, a biotechnology company developing ...

University of Bristol researchers have discovered a VEGF-C gene therapy that protects the kidneys in people with type 1 ...

Onasemnogene abeparvovec gene therapy post-nusinersen or risdiplam showed meaningful motor improvements in children with SMA, with a manageable safety profile. The study cohort included older, heavier ...

CRISPR, short for Clustered Regularly Interspaced Short Palindromic Repeats, is a revolutionary gene-editing tool originally discovered as a bacterial defence mechanism. Scientists have repurposed it ...