Long-term follow-up shows 95% success rate, no serious complications in largest ADA-SCID gene therapy study to date ...
Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...
Adam Feuerstein is a senior writer and biotech columnist, reporting on the crossroads of drug development, business, Wall Street, and biotechnology. He is also a co-host of the weekly biotech podcast ...
9don MSNOpinion
What the US can learn from Europe when it comes to the provision of cell and gene therapy
There are currently no available treatment options for more than 90% of the approximately 7,000 rare diseases identified to ...
Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...
A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two ...
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